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International experience with performance-based risk-sharing arrangements: implications for the Chinese innovative pharmaceutical market

Published online by Cambridge University Press:  23 September 2020

Weiwei Xu Open the ORCID record for Weiwei Xu [Opens in a new window]  and
Jing Wu Open the ORCID record for Jing Wu [Opens in a new window]
Weiwei Xu
Affiliation:
GongJing Healthcare Ltd., Nanjing, China
Jing Wu
Affiliation:
School of Pharmaceutical Science and Technology, Tianjin University, Tianjin, China
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Abstract

Objectives

Various forms of outcomes-based or risk-sharing agreements have been implemented since early 2000s as a way of access to innovative medicinal products. This study aims to summarize the international experience of performance-based risk-sharing arrangements (PBRSAs) and identify the preconditions for a successful implementation of such schemes. Their implications for the Chinese healthcare market are discussed.

Methods

A systematic literature review (in PubMed) was conducted to review the evidence on the nature and performance of PBRSAs in the past 10 years. Grey literature was searched for reports in government websites of the countries in scope.

Results

The search identifies 463 records from PubMed and 3 additional records from other sources. Thirty-one publications are included in the final review. The following preconditions were identified to support a successful implementation of PBRSAs: (1) Identify meaningful and feasible outcome measurements; (2) Establish an effective and efficient data collection infrastructure; (3) Control of the implementation costs; (4) Develop governance and administrative infrastructure to allow delisting and rebate/refund; (5) Clarify personal data protection issues.

Conclusions

The implementation of PBRSAs has proven to be challenging. Although the Chinese healthcare system is not yet well equipped to implement such schemes, some recent changes may pave the way to successful PBRSAs for particular innovative products.

Keywords

Performance-based risk-sharing agreementImplementationPreconditionsChina
Type
Assessment
Information
International Journal of Technology Assessment in Health Care , Volume 36 , Issue 5 , October 2020 , pp. 486 - 491
Copyright
Copyright © The Author(s), 2020. Published by Cambridge University Press

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